Pharming

Cancer research
#Clinical trials #Paediatrics #Pharming #Phase III trial #Rare disease

Trials investigate targeted APDS treatment in a paediatric setting

The first patient has been dosed in a Phase III study evaluating a paediatric granulated formulation of leniolisib in children with activated phosphoinositide 3-kinase delta syndrome (APDS). Pharming’s investigational drug leniolisib is an oral, selective phosphoinositide 3-kinase delta (PI3Kδ) inhibitor. At sites in the… Read More

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